Conditions Treatable by Stem Cell Transplantation

Diseases Treatable by Stem Cell Transplantation
Compilation from The National Donor Program, 2002 and www.stemcelltherapies.org, 2004

Stem Cell Disorders

Aplastic Anemia (Severe)
Fanconi Anemia
Paroxysmal Nocturnal Hemoglobinuria (PNH)

Acute Leukemias

Acute Lymphoblastic Leukemia (ALL)
Acute Myelogenous Leukemia (AML)
Acute Biphenotypic Leukemia
Acute Undifferentiated Leukemia

Chronic Leukemias

Chronic Myelogenous Leukemia ( CML)
Chronic Lymphocytic Leukemia (CLL)
Juvenile Chronic Myelogenous Leukemia (JCML)
Junveile Myelomonocytic Leukemia (JMML)

Myeloproliferative Disorders

Acute Myelofibrosis
Agnogenic Myeloid Metaplasia
(myelofibrosis)
Polycythemia Vera
Essential Thrombocythemia

Myelodysplastic Syndromes

Refractory Anemia (RA)
Refractory Anemia with Ringed Sideroblasts (RARS)
Refractory Anemia with Excess Blasts (RAEB)
Refractory Anemia with Excess Blasts in Transformation (RAEB-T)
Chronic Myelomonocytic Leukemia (CMML)
Lymphoproliferative Disorders
Non-Hodgkin's Lymphoma
Hodgkin's Disease
Prolymphocytic Leukemia
Inherited Erythrocyte Abnormalities
Beta Thalassemia Major
Pure Red Cell Aplasia
Sickle Cell Disease

Liposomal Storage Diseases

Mucopolysaccharidoses (MPS)
Hurler's Syndrome (MPS-IH)
Scheie Syndrome (MPS-IS)
Hunter's Syndrome (MPS-II)
Sanfilippo Syndrome (MPS-III)
Morquio Syndrome (MPS-IV)
Maroteaux-Lamy Syndrome (MPS-VI)
Sly Syndrome, Beta-Glucuronidase Deficiency (MPS-VII)
Adrenoleukodystrophy
Mucolipidosis II (I-cell Disease)
Krabbe Disease
Gaucher's Disease
Niemann-Pick Disease
Wolman Disease
Metachromatic Leukodystrophy

Histiocytic Disorders

Familial Erythrophagocytic Lymphohistiocytosis
Histiocytosis-X
Hemophagocytosis

Phagocyte Disorders

Chediak-Higashi Syndrome
Chronic Granulomatous Disease
Neutrophil Actin Deficiency
Reticular Dysgenesis

Inherited Platelet Abnormalities

Amegakaryocytosis/Congenital
Thrombocytopenia

Plasma Cell Disorders

Multiple Myeloma
Plasma Cell Leukemia
Waldenstrom's Macroglobulinemia

Other Malignancies

Breast Cancer
Ewing Sarcoma
Neuroblastoma
Renal Cell Carcinoma

Lung Disorders

COPD
Bronchial Asthma

Congenital Immune System Disorders

Ataxia-Telangiectasia
Kostmann Syndrome
Leukocyte Adhesion Deficiency
DiGeorge Syndrome
Bare Lymphocyte Syndrome
Omenn's Syndrome
Severe Combined Immunodeficiency (SCID)
SCID with Adenosine Deaminase Deficiency
Absence of T & B Cells SCID
Absence of T Cells, Normal B Cell SCID
Common Variable Immunodeficiency
X-Linked Lymphoproliferative Disorder

Other Inherited Disorders

Lesch-Myhan Syndrome
Cartilage-Hair Hypoplasia
Glanzmann Thrombasthemia
Osteopetrosis

Neurological Conditions

Acute and Chronic Stroke
Traumatic Brain Injury
Cerebral Palsy
Multiple Sclerosis
Amyotrophic lateral sclerosis (ALS)
Cognitive Dysfunction
Epilepsy
Depression

Heart Conditions

Atherosclerosis
Congestive Heart Failure
Myocardial Infarction

Metabolic Disorders

Diabetes

Eye Disorders

Macular Degeneration
Optic Atrophy

Alphabetical Listing

back
next
This information is presented for educational purposes only.



©Copyright 2004-2008 Stem Cell Therapies All Rights Reserved
For more information feel free to Contact Us


Sitemap